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Correction of Beta-Thalassemia IVS-II-654 Mutation in a Mouse Model Using Prime Editing
Authors:Haokun Zhang  Ruilin Sun  Jian Fei  Hongyan Chen  Daru Lu
Affiliation:1.State Key Laboratory of Genetic Engineering, MOE Engineering Research Center of Gene Technology, School of Life Sciences, Fudan University, Shanghai 200438, China;2.Shanghai Model Organisms Center, No.3577 Jinke Rd., Shanghai 201203, China; (R.S.); (J.F.);3.NHC Key Laboratory of Birth Defects and Reproductive Health, Chongqing Key Laboratory of Birth Defects and Reproductive Health, Chongqing Population and Family Planning, Science and Technology Research Institute, Chongqing 404100, China
Abstract:
Keywords:prime editing  beta-thalassemia  IVS-II-654 mutation  genome editing  gene therapy
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